Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases, today announced the ...

Families with Huntington’s need this to be true more than most. The devastating neurodegenerative disease is caused by a CAG ...

Advances delivered what may feel like medical miracles, including the first bladder transplant, a lifesaving personalized ...

For the first time, scientists have successfully treated someone suffering from Huntington's disease, a fatal genetic illness ...

LQT-23 is a potent, highly differentiated, first-in-class allosteric small molecule inhibitor of MSH3/MutSß Unique mechanism of action with potential to slow or stop ...

LoQus23 Therapeutics, based at Granta Park in Cambridge, has stepped up its bid to combat Huntington’s Disease (HD). It has ...

Researchers have implicated a new gene in the progression of Huntington's disease in a brain organoid model. The gene may contribute to brain abnormalities much earlier than previously thought. Six ...

UCL and uniQure report the first treatment to slow Huntington’s disease with gene therapy AMT-130. High-dose patients had 75% less progression over three years compared with standard care. uniQure ...

An experimental gene therapy has become the first treatment to successfully slow the progression of Huntington’s disease. While the findings are still preliminary, the approach could be a major ...

Huntington's Disease burdens caregivers in India, facing financial strain and limited support amid widespread underdiagnosis ...

Huntington’s disease is a genetic disease that is debilitating and progressive leading to severe brain damage and eventual death. In patients with this autosomal dominant disease, there is presence of ...

In many respects, Huntington’s disease is the epitome of a well-understood hereditary disease. The condition was comprehensively described almost a century and a half ago 1. Its symptoms are ...