BridgeBio Pharma’s experimental drug for the most common cause of dwarfism accelerated children’s growth in a pivotal clinical trial.
Feb 12 (Reuters) - BridgeBio Pharma said on Thursday its experimental therapy boosted growth rates in children with a rare ...
BridgeBio is hoping infigratinib will get another shot at approval after the medicine hit the key goals of a phase 3 study in ...
The Food and Drug Administration approved the first treatment for the most common cause of dwarfism Friday, a drug that has proved to increase children’s height but has been polarizing among adults ...
Diastrophic dysplasia (DTD) is a type of skeletal dysplasia, a group of conditions often resulting in dwarfism. DTD may cause a person to have short stature and very short arms and legs. DTD is ...
A genetic disorder that slows bone growth and leads to dwarfism now has an approved drug, a biologic therapy developed by BioMarin Pharmaceutical. The European Commission decision announced Friday ...
Zach and Tori Roloff have revealed their newborn son, Josiah, has been diagnosed with achondroplasia, a form of dwarfism. In an exclusive interview with Us Weekly, the "Little People, Big World" ...
People have been riveted by Hulu's "Good American Family," which tells the complex and devastating story of Natalia Grace. As the drama series shows, Grace was a Ukrainian orphan with a rare form of ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results